AviadoBio Bets on Blood-Brain Barrier Technology in Push for One-Time Alzheimer's Treatment
A licensing deal with Apertura Gene Therapy gives the London-based biotech a clinically validated delivery system to pair with its gene-silencing platform, but the hard work is still ahead.
Andelyn Biosciences and Evolyra Therapeutics Join Forces to Advance Gene Therapies for Limb-Girdle Muscular Dystrophy
A new CDMO partnership aims to bring clinical-grade AAV gene therapies to patients with LGMD types 2C and 2D, with an IND filing targeted for the second half of 2026
PRISM ALS Sets Out to Improve ALS/MND Drug Discovery
A new international collaboration is building more representative stem cell models of ALS, an effort that could improve drug discovery and reduce clinical trial failure rates.